Gene therapy for inherited diseases

Tue 4 February 2020

School of Clinical Medicine

James M. Wilson, MD, PhD
Rose H. Weiss Professor and Director, Orphan Disease Center
Professor of Medicine and Pediatrics
Director, Gene Therapy Program
Perelman School of Medicine, University of Pennsylvania

Advisor and Co-Founder of Scout Bio and Passage Bio
Co-Founder of Surmount Bio

James M. Wilson, MD, PhD, is a Professor in the Perelman School of Medicine at the University of Pennsylvania where he has led an effort to develop the field of gene therapy. His research career spanning over 40 years has focused on rare diseases and ways to treat them by gene therapy. The Wilson lab identified a new type of vector based on novel isolates of adeno-associated viruses which have become best in class for gene therapy being used by over 29 companies. More recently Dr. Wilson’s laboratory has focused on improved vectors for gene therapy and clinical applications of genome editing and mRNA therapy.

Cost: Free